, also known as Stargardt's macular dystrophy, affects the area of the retina called the macula and causes a reduction in central vision.
This pipeline also contains several other molecules for genetic eye diseases, including QR-411 for Usher syndrome type 2A due to the PE-40 mutation, QRX-1011 for Stargardt's disease
and QRX-504 for Fuchs endothelial corneal dystrophy.
It can also assist in the diagnosis and management of patients with hereditary conditions such as Best's and Stargardt's disease
Leeds-based Laura was diagnosed with Stargardt's disease
, a rare inherited condition, which causes the light-sensitive cells in the retina to deteriorate, resulting in central vision loss or, in some cases, total blindness.
Victoria, 31, has Stargardt's disease
, an inherited eye disease which affects the macula.
and age-related macular degeneration are different diseases with similar symptoms.
In conjunction, the company intends to initiate both its pivotal programme for Stargardt's disease
(SMD) and Phase Two age-related macular degeneration (AMD) trials using its retinal pigment epithelium (RPE) cells to determine the efficacy and safety, as well as to assess relevant functional and anatomical parameters of cell transplantation using an untreated control group, with the intent of bringing a product to market potentially as early as 2019.
Its lead product is undergoing studies in humans who have dry age-related macular degeneration and Stargardt's disease
or Stargardt's macular dystrophy is a genetic disease that causes progressive vision loss, usually starting in children between 10 to 20 years of age.
The Scots both suffer from a deteriorating eye condition called Stargardt's disease
Smyth, who has limited vision because of Stargardt's disease
, was not challenged as he burst from the blocks.
Boss was diagnosed with Stargardt's disease
, a genetic disorder that led to blindness when she was just eight-years-old.